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FDA Grants Priority Review of Biologics License Application for beti-cel Gene Therapy for Patients with I[superscript two]-thalassemia Who Require Regular Red Blood Cell Transfusions. Nov 24, 2021 761
SMILE DEFIES THE DOCS - BUT OLIVIA-MAY NEEDS A MIRACLE TO SAVE LIFE; Mum's desperate bid to raise cash for gene therapy in the US to save terminally ill girl. EXCLUSIVE MIKE LOCKLEY Sunday Mercury Writer Nov 21, 2021 528
Sanofi Commits to Investment of Up to USD 60m in Gene Therapy Company Gyroscope Therapeutics. Nov 8, 2021 485
Avrobio Receives Rare Pediatric Disease Designation from the US FDA for AVR-RD-05, a Gene Therapy for Mucopolysaccharidosis Type II or Hunter Syndrome. Nov 5, 2021 310
Sio Gene Therapies announces FDA granted Fast Track Designation to AXO-AAV-GM2. Nov 1, 2021 206
CANbridge Pharmaceuticals Enters into Duchenne Muscular Dystrophy Gene Therapy Research Agreement with University of Washington School of Medicine. Nov 1, 2021 294
Taysha announces AAV -based gene therapy approach fo AS treatment. Oct 25, 2021 244
Homology Medicines announces presentations across gene therapy programs. Oct 21, 2021 353
Sio Gene Therapies presents interim data from AXO-AAV-GM1 trial at ESGCT. Oct 21, 2021 470
Voyager Therapeutics presents preclinical data on GBA1 gene therapy. Oct 20, 2021 221
Oxford says Boehringer Ingelheim exercises option on gene therapy treatment. Oct 19, 2021 287
Avrobio reports safety data across gene therapies for Fabry, Gaucher disease. Oct 19, 2021 179
uniQure announces presentations at ESGCT annual meeting. Oct 19, 2021 422
Athenex, Center for Cell and Gene Therapy announce allowance of first US patent. Oct 18, 2021 179
PTC Therapeutics opens New Jersey gene therapy manufacturing facility. Oct 15, 2021 204
PTC Therapeutics opens New Jersey gene therapy manufacturing facility. Oct 15, 2021 205
Gene Therapy Works Better Than Stem Cells In Restoring Vision After Stroke. Oct 11, 2021 408
Taysha gets option from UTSW to license AAV9 gene therapy for CLN7 disease. Oct 5, 2021 326
Taysha Obtains Exclusive Option from UTSW to License Worldwide Rights to Clinical-Stage AAV9 Gene Therapy Program for CLN7 Disease. Oct 5, 2021 772
Regenerative Materials in Periodontics: A Review. Vamsi, E. Santosh; Ramesh, K.S.V.; Penmetsa, Gautami S.; Sruthima, N.V.S.; Kumar, P. Mohan; Bypalli, Oct 1, 2021 4297
Taysha Gene Therapies Receives Orphan Drug Designation from the European Commission for TSHA-101 for the Treatment of Infantile GM2 Gangliosidosis. Sep 30, 2021 432
Gyros Protein Technologies Introduces Gyrolab AAV9 Titer Kit to Support AAV-Based Cell and Gene Therapy Production. Sep 30, 2021 293
Taysha Gene Therapies gets orphan drug designation from EC for TSHA-101. Sep 29, 2021 316
PTC Therapeutics' gene therapy shows improvement in childer with AADC. Sep 29, 2021 189
Boston Labs, Germfree Launch Mobile Cell and Gene Therapy Manufacturing Platform. Sep 22, 2021 234
Seneca Therapeutics Launches Novel Cancer Gene Delivery Platform based on SVV-001 Technology. Sep 22, 2021 399
Bluebird Bio submits BLA to FDA for beti-cel gene therapy. Sep 21, 2021 155
US FDA Clears IND for Neurogene's NGN-101 Gene Therapy to Treat CLN5 Batten Disease. Sep 15, 2021 439
Sio Gene Therapies doses first infantile patient in gene therapy study. Clinical report Sep 9, 2021 169
UK MHRA Grants GenSight Biologics' Lumevoq Ophthalmic Gene Therapy Promising Innovative Medicine Designation. Sep 8, 2021 575
GenSight's LUMEVOQ ophthalmic gene therapy wins Promising Innovative Medicine (PIM) designation in the UK. Sep 7, 2021 214
NeuExcell Therapeutics partners with Spark Therapeutics to develop novel gene therapy for Huntington's Disease. Sep 7, 2021 217
GenSight's LUMEVOQ ophthalmic gene therapy wins Promising Innovative Medicine (PIM) designation in the UK. Sep 7, 2021 215
NeuExcell Therapeutics partners with Spark Therapeutics to develop novel gene therapy for Huntington's Disease. Sep 7, 2021 218
Hope for sick babies as tot given world's most expensive drug 'has been reborn'; Edward Willis-Hall as a rare genetic condition called type one spinal muscular atrophy which often ends in death before the age of two but £1.79million pioneering gene therapy Zolgensma has seen him 'reborn'. By, Natasha Wynarczyk Sep 7, 2021 968
First Patient Dosed in the United States with LYS-GM101 Investigational Gene Therapy for the Treatment of GM1 Gangliosidosis. Aug 30, 2021 354
Taysha Gene Therapies Receives Orphan Drug Designation for TSHA-105 for the Treatment of Epilepsy Caused by SLC13A5 Deficiency from the European Commission. Aug 27, 2021 231
Taysha Gene Therapies gets ODD for TSHA-105 for epilepsy by the EC. Aug 25, 2021 177
Taysha Gene Therapies reports Q2 EPS ($1.09), consensus (84c). Financial report Aug 16, 2021 269
Sio Gene Therapies provides information on upcoming milestones. Aug 12, 2021 157
Sarepta executes licensing agreement for gene therapy program. Aug 4, 2021 226
ASC Therapeutics Partners with University of Massachusetts Medical School to Co-Develop Novel Gene Therapy for Maple Syrup Urine Disease. Jul 30, 2021 632
ASC Therapeutics partners with the University of Massachusetts Medical School to co-develop novel gene therapy for Maple Syrup Urine Disease. Jul 28, 2021 192
ASC Therapeutics partners with the University of Massachusetts Medical School to co-develop novel gene therapy for Maple Syrup Urine Disease. Jul 28, 2021 193
XyloCor Therapeutics Commences Phase 2 Component of Phase 1/2 EXACT Clinical Study of XC001 Gene Therapy for Refractory Angina. Clinical report Jul 28, 2021 672
Selecta Biosciences appoints Jude Samulski as gene therapy special advisor. Jul 26, 2021 255
Bluebird bio Receives EC Approval for Skysona Gene Therapy for Patients Less Than 18 Years of Age with Early Cerebral Adrenoleukodystrophy Without Matched Sibling Donor. Jul 22, 2021 784
Gene Therapy Specialist Kriya Therapeutics Raises USD 100m in Series B Financing. Jul 16, 2021 478
Lysogene Receives FDA Fast Track Designation for LYS-GM101 Gene Therapy for the Treatment of GM1 Gangliosidosis. Jul 12, 2021 415
Lysogene reports FDA fast track designation for LYS-GM101 gene therapy. Jul 8, 2021 201
DOCTORS DEBUNK THE MEDICAL "CONSENSUS": Doctors worldwide are speaking out against government lockdowns and vaccine mandates, while being ignored and attacked by the media. Terrell, Rebecca Cover story Jul 5, 2021 2057
'Amazing' UCD in skin disease breakthrough; New gene therapy to transform lives of people living with painful condition. JAMES WARD Jul 5, 2021 523
'£1.8million jab helped tiny Arthur -- and babies should be saved at any cost'; Dr Miriam Stoppard looks into the groundbreaking new gene therapy for spinal muscular atrophy, which could help up to 80 children every year. By, Miriam Stoppard Jul 5, 2021 469
Everads Therapy collaborates with clinical-stage gene therapy company. Jul 1, 2021 193
Everads Therapy collaborates with clinical-stage gene therapy company. Jul 1, 2021 192
AKU wins grant to develop gene therapies for blood disorders. Jul 1, 2021 486
EMA Grants Orphan Drug Designation to CLN5 Batten Disease Gene Therapy. Jun 29, 2021 459
LATEST COMPANY NEWS. Jun 24, 2021 18278
Grace Science Receives US FDA Orphan Drug Designation for GS-100, an AAV9 Gene Therapy for NGLY1 Deficiency. Jun 22, 2021 315
Family in heartbreaking wait to see if their baby can get life-saving gene therapy drug; Baby Jenson Burton's diagnosis came as a shock to the family-of-five and has caused him to be a "floppy baby" who cannot sit or walk and must be fed through his stomach. By, Andrew Topping & Graeme Murray Jun 20, 2021 593
Bayer to Advance Two First-of-its-Kind Investigational Cell and Gene Therapies for Parkinson's Disease. Jun 10, 2021 470
Codexis, Takeda expand collaboration, license agreement for gene therapy. Jun 10, 2021 215
Sio Gene Therapies reports Q4 EPS (5c), consensus (17c). Financial report Jun 9, 2021 219
Agonising wait for £1.8million miracle drug to save baby Edward as 50 tots face delay; EXCLUSIVE: After baby Arthur Morgan last Tuesday became the first in England to receive pioneering gene therapy drug Zolgensma, now around 50 other families face an agonising wait after being given the devastating news that their newborn has Type 1 spinal muscular atrophy. By, Martin Bagot Jun 3, 2021 949
Baby, 5-months-old, first to be given 'revolutionary' gene therapy treatment on the NHS; Babies with severe cases of SMA rarely live beyond two. By, Ruby Gregory Jun 3, 2021 528
'NHS will give gift of life if politicians and the public give the tools and funds'; US gene therapy is further proof that medical science is an overwhelming force for good -after Covid, scientists and the NHS will give us the gift of life if politicians and the public give them the tools and funds to do the job. By, Voice of the Mirror Jun 1, 2021 374
Citius Pharmaceuticals honoured with Best Poster Award at International Society for Cell and Gene Therapy 2021 Annual Meeting. May 26, 2021 212
Citius Pharmaceuticals honoured with Best Poster Award at International Society for Cell and Gene Therapy 2021 Annual Meeting. May 26, 2021 211
Blind man's sight partially restored using pioneering gene therapy; The 58-year-old man was able to recognise objects with the aid of light-stimulating goggles. By, Nilima Marshall (PA) & Erin Santillo May 25, 2021 573
Bluebird bio Receives Positive CHMP Opinion for Skysona Gene Therapy for Patients Less Than 18 Years of Age with Early Cerebral Adrenoleukodystrophy. May 21, 2021 921
Biogen, Gingko Bioworks enter gene therapy collaboration, license agreement. May 21, 2021 186
Biogen, Gingko Bioworks enter gene therapy collaboration, license agreement. May 21, 2021 236
Tenaya Therapeutics Receives Orphan Drug Designation and Presents Pre-Clinical Data for its Most Advanced Gene Therapy Product Candidate for Genetic Hypertrophic Cardiomyopathy. May 20, 2021 404
Otonomy, AGTC present preclinical results for OTO-825 gene therapy. May 14, 2021 196
Rocket Pharmaceuticals presents gene therapy program data at ASGCT. May 13, 2021 308
Sio Gene Therapies announces data from clinical trial studying AXO-AAV-GM1. Clinical report May 13, 2021 438
uniQure presents clinical data from phase III HOPE-B gene therapy trial. May 13, 2021 304
Tora was saved by world's most expensive treatment; Danny Buckland hears about a revolutionary gene therapy costing [euro]2million per patient, which has been described as a 'miracle'. Danny Buckland May 11, 2021 997
Tora was saved by world's most expensive treatment; Danny Buckland hears about a revolutionary gene therapy costing PS1.79million per patient, which is now available on the NHS. Danny Buckland May 11, 2021 995
Taysha Gene Therapies announces publication of preclinical data for TSHA-102. May 10, 2021 340
Genprex in-licenses additional gene therapy technologies to treat non-small cell lung cancer. May 7, 2021 276
Genprex in-licenses gene therapy technologies for lung cancer treatment. May 6, 2021 161
Lantheus Grants Allegheny Health Network Exclusive Rights for the Use of its Microbubbles in Combination with Ultrasound Assisted Gene Therapy for the Development of a Proposed Treatment for Xerostomia. May 3, 2021 587
Injectable Scaffold. May 1, 2021 475
Sharpening the focus on the mission to make the impossible possible - Claudia Cavalluzzo; When I was still studying at university in the early 2000s, gene therapy was described as the 'magic bullet'. It was considered a fantasy that scientists were continually pursuing, despite their constant failures. Fast forward almost 20 years and today, gene therapy has become a recognised part of our lives, as a well-known strategy to fight Covid-19. Claudia Cavalluzzo Apr 28, 2021 593
Ascheim Named Chief Medical Officer at StrideBio. Apr 27, 2021 415
uniQure announces removal of clinical hold on hemophiilia B gene therapy program. Apr 26, 2021 313
Marks, Paulk Named to Dyno Therapeutics Scientific Advisory Board. Apr 26, 2021 364
During to Join the Scientific Advisory Board of Brooklyn ImmunoTherapeutics. Apr 26, 2021 307
US FDA Clears Apic Bio IND Application for Lead Gene Therapy Candidate APB-102 for the Treatment of SOD1 ALS. Apr 22, 2021 446
Krystal Biotech provides update on its studies of KB407, KB408. Apr 19, 2021 443
StrideBio Inks Multi-technology License and Master SRA with Duke University to Advance Next-generation Gene Therapies. Apr 15, 2021 671
Jaguar Gene Therapy gains $139 million from investors. Apr 14, 2021 171
Genprex targets non-small cell lung cancer and diabetes via gene therapy. Apr 13, 2021 780
Mirum Pharmaceuticals and Vivet in pact for Vivet's gene therapy. Apr 12, 2021 274
Genprex targets non-small cell lung cancer and diabetes via gene therapy. Apr 7, 2021 773
TRANSGENIC TECHNOLOGY IN LIVESTOCK: CURRENT STATUS AND FUTURE HORIZONS. M. Shaukat, H. Shaukat, S. G. Mohy-ud-Din, R. Akram, S. Ali, R. Rafique, H. M. Waqar, Z. Afzal, A. W Mar 31, 2021 6537
Researchers; see cellular Benefits Of Gene Therapy Decades After Treatment. Mar 29, 2021 397
uniQure announces findings from case of HCC in Hemophilia B gene therapy program. Mar 29, 2021 394
XyloCor Therapeutics Completes Oversubscribed USD 41.9m Series A Financing to Advance Novel Gene Therapy Pipeline for Coronary Artery Disease. Mar 23, 2021 744
Bluebird Bio Presents Long-Term Data for Elivaldogene Autotemcel Gene Therapy for Cerebral Adrenoleukodystrophy. Mar 16, 2021 914
Tevogen Bio Forges Partnership with BioCentriq, New Jersey Innovation Institute's Cell and Gene Therapy Center, to Enhance Tevogen's Development Capacity of Its Proprietary Targeted T Cell Therapy For COVID-19. Mar 16, 2021 249
Orgenesis leads the charge at an exciting time for cell and gene therapy. Mar 10, 2021 1229
WuXi AppTec UK Gene Therapy Technologies Specialist Oxgene. Mar 3, 2021 221
WuXi AppTec UK Gene Therapy Technologies Specialist Oxgene. Mar 3, 2021 198
Abu Dhabi's Burjeel Hospital provides transformational gene therapy. Mar 1, 2021 553
Gene therapy launch. Feb 26, 2021 471
Jaguar Gene Therapy launches in Lake Forest. Feb 26, 2021 182
Jaguar Gene Therapy Launches with Goal of Accelerating Breakthroughs in Gene Therapy for Patients Suffering from Severe Genetic Diseases. Feb 25, 2021 636
Kolon Life executives acquitted of falsifying data of gene therapy drug. Feb 19, 2021 322
Bluebird bio Temporarily Suspends Phase 1/2 and Phase 3 Studies of LentiGlobin Gene Therapy for Sickle Cell Disease. Clinical report Feb 17, 2021 889
Lysogene Receives FDA Clearance of Investigational New Drug Application to Initiate the Gene Therapy Clinical Trial in the US with LYS-GM101 for the Treatment of GM1 Gangliosidosis. Feb 16, 2021 422
Gyroscope Therapeutics Touts Positive Interim Data from Phase I/II FOCUS Trial of Investigational Gene Therapy GT005. Feb 16, 2021 540
Sensorion Forges Third Gene Therapy Collaboration with Institut Pasteur. Feb 16, 2021 541
Avrobio Touts 100% Kidney Substrate Reduction at 12 Months Post-Gene Therapy in First Patient Dosed with plato Gene Therapy Platform in Fabry Disease Phase 2 Trial. Feb 9, 2021 262
Taysha Gene Therapies Forges Collaborations with Cleveland Clinic and UT Southwestern Gene Therapy Program. Feb 9, 2021 160
Importance of Genetic Engineering and Gene Therapy in the Management of Viral Diseases and Outbreaks. Arora, Vanshika; Aggarwal, Ashim; Aggarwal, Shivani; Kumar, Randhir Feb 8, 2021 3238
Nanobiotix partners with Sanofi for utilising Nanoprimer technology as promising option to improve gene therapy. Jan 26, 2021 232
Nanobiotix partners with Sanofi for utilising Nanoprimer technology as promising option to improve gene therapy. Jan 26, 2021 228
Chinese scientists develop gene therapy which could delay ageing. Reuters News Service Jan 20, 2021 396
Scientists create 'age reversing therapy' extending life of mice -it may work on humans; The method was detailed in a paper in the Science Translational Medicine journal and experts say the anti-ageing developments in new gene therapy could one day be used on humans. By, William Walker Jan 20, 2021 419
Chinese scientists develop gene therapy which could delay aging. Jan 20, 2021 449
Selection cements region as global bio-science hub; Centre TO OFFER TRAINING FOR GENE THERAPY WORK. JONATHON MANNING jonathon.manning@reachplc.com @JONNYAMANNING Jan 19, 2021 446
Ixaka Launches as an Integrated Cell and Gene Therapy Company. Jan 19, 2021 699
BioMarin Reports Positive Phase 3 Gene Therapy Trial Results. Jan 11, 2021 165
Almirall collaborates with Tyris Therapeutics for gene therapy development. Jan 8, 2021 154
Almirall collaborates with Tyris Therapeutics for gene therapy development. Jan 8, 2021 158
Pfizer Doses First Participant in Phase 3 Study for Duchenne Muscular Dystrophy Investigational Gene Therapy. Jan 7, 2021 581
AllStripes Forges Collaboration with Taysha Gene Therapies for SURF1-Associated Leigh Syndrome Programme. Jan 5, 2021 253
miR-451 on Myocardial Ischemia-Reperfusion in Rats by Regulating AMPK Signaling Pathway. Guo, Yulin; Gao, Jie; Liu, Yan; Zhang, Xitao; An, Xiangguang; Zhou, Jian; Su, Pixiong Jan 1, 2021 7112
Emerging Patent Landscape for Gene Therapy as a Potential Cure for COVID-19. Zhou, Wuyuan; Chen, Deng Report Jan 1, 2021 3075
Advances in Magnetic Nanoparticle-Driven Delivery of Gene Therapies towards Prostate Cancer. Panday, Raju; Abdalla, Ahmed M. E.; Neupane, Manisha; Khadka, Sujan; Kricha, Aymane; Yang, Guang Jan 1, 2021 8146
Programmed Cell Death Ligand 1-Transfected Mouse Bone Marrow Mesenchymal Stem Cells as Targeted Therapy for Rheumatoid Arthritis. Hu, Qiong-ying; Yuan, Yun; Li, Yu-chen; Yang, Lu-yao; Zhou, Xiang-yu; Xiong, Da-qian; Zhao, Zi-yi Jan 1, 2021 5275
Amryt Pharma treatment awarded US orphan status for fragile skin condition. Dec 24, 2020 317
Amryt Pharma treatment awarded US orphan status for fragile skin condition. Dec 24, 2020 315
LG Chem to develop cell, gene therapy. Dec 23, 2020 292
Gyroscope Therapeutics and the University of Pennsylvania Announce Research Agreement to Develop Gene Therapies for Serious Eye Diseases. Dec 21, 2020 521
Bahrain 'could take lead in sickle cell gene therapy'. Dec 20, 2020 554
Genprex Completes Manufacturing Technology Transfer for Novel Gene Therapy. Dec 8, 2020 438
Tevard Biosciences collaborates with Zogenix to identify and produce tRNA-based gene therapies. Dec 4, 2020 219
Tevard Biosciences collaborates with Zogenix to identify and produce tRNA-based gene therapies. Dec 4, 2020 223
Orgenesis leads the charge at an exciting time for cell and gene therapy. Dec 3, 2020 1634
First Patient Received Investigational Gene Therapy GT005 Via Orbit Subretinal Delivery System in Ongoing Phase I/II FOCUS Trial. Oct 28, 2020 368
Bayer Buys US Cell And Gene Therapy Firm AskBio For Up To USD4 Billion. Oct 26, 2020 428
Ultragenyx, Solid Biosciences collaborate for DMD gene therapies. Oct 23, 2020 371
Homology uveils in vivo gene therapy development program for Hunter Syndrome. Oct 22, 2020 193
Dyno Therapeutics Enters Collaboration and License Agreement with Roche to Develop Next-Generation AAV Gene Therapy Vectors for CNS Diseases and Liver-Directed Therapies. Oct 19, 2020 451
Pfizer, Sangamo Dose First Participant in Phase 3 Study Evaluating Hemophilia A Gene Therapy Treatment. Oct 7, 2020 629
Avrobio Expands Lentiviral Gene Therapy Pipeline with Program for Hunter Syndrome. Oct 5, 2020 757
Pfizer Receives FDA Fast Track Designation for Duchenne Muscular Dystrophy Investigational Gene Therapy. Oct 2, 2020 345
European Medicines Agency's Accepts bluebird Marketing Authorization Application for elivaldogene autotemcel Gene Therapy for Cerebral Adrenoleukodystrophy. Oct 2, 2020 546
Avrobio Receives Orphan Drug Designation from the European Medicines Agency for AVR-RD-02, an Investigational Gene Therapy for Gaucher Disease. Sep 28, 2020 476
Taysha Gene Therapies prices IPO at USD20.00 per share. Sep 25, 2020 156
Clearside Biomedical announces data presentations at The Retina Society 2020. Sep 23, 2020 632
Vivet Therapeutics and Pfizer Enter into Manufacturing Agreement for Vivet's Investigational Gene Therapy for Wilson Disease. Sep 23, 2020 408
European Medicines Grants Priority Medicines Designation to bluebird bio's LentiGlobin for Sickle Cell Disease Gene Therapy. Sep 23, 2020 430
Gyroscope Therapeutics Granted FDA Fast Track Designation for GT005, an Investigational Gene Therapy for Dry Age-Related Macular Degeneration. Sep 22, 2020 300
Mustang Bio announces Orphan Drug Designation for MB-207. Sep 22, 2020 370
Passage Bio announces publication of preclinical gene therapy study data. Sep 17, 2020 358
Amryt Pharma set to receive orphan designation for pre-clinical skin treatment. Sep 16, 2020 335
Orgenesis leads the charge at an exciting time for cell and gene therapy. Sep 5, 2020 1264
Edinburgh biotech creating 'high-value' jobs after multi-million funds boost; An Edinburgh-based gene therapy specialist is making a multi-million-pound investment in a move that will create "high-value" jobs in the capital. Scott Reid Sep 2, 2020 530
Gene Therapy to Reverse Aging: Harvard's Dr. George Church is pioneering a way to help turn back the aging clock. Fan, Shelly Xuelai Interview Sep 1, 2020 1261
bluebird bio Presents New Results from Clinical Development Program of elivaldogene autotemcel Gene Therapy for Cerebral Adrenoleukodystrophy. Sep 1, 2020 1147
A review on brain-derived neurotrophic factor and its role in depression and anxiety. Iacob, Vlad Teodor; Palimariciuc, Matei; Chirita, Vasile; Chirita, Roxana Sep 1, 2020 3632
FinnCap touts cell and gene therapy as next wave of innovation in pharma industry. Aug 27, 2020 659
BioMarin receives FDA CRL for BLA for valoctocogene roxaparvovec gene therapy. Aug 19, 2020 233
4D Molecular Therapeutics Receives FDA Fast Track Designation for 4D-310 Gene Therapy for Treatment of Fabry Disease. Aug 13, 2020 469
Gyroscope Therapeutics Initiates Phase II Programme Evaluating its Investigational Gene Therapy, GT005, for Dry Age-Related Macular Degeneration. Aug 13, 2020 671
Ocugen receives Orphan Drug designation for OCU400 gene therapy. Aug 10, 2020 387
Aminoglycosides: From Antibiotics to Building Blocks for the Synthesis and Development of Gene Delivery Vehicles. Bellucci, Maria Cristina; Volonterio, Alessandro Aug 1, 2020 12754
Ocugen granted Orphan Drug Designation for OCU-400 gene therapy. Jul 27, 2020 268
Genprex advisor George Gittes wins $2.6 million NIH grant to develop diabetes gene therapy, GPX-002. Jul 22, 2020 378
PreveCeutical advances Dual Gene Therapy Research Program combatting Type 2 diabetes and obesity. Jul 16, 2020 382
First Patient Treated in Phase 1 Trial of RP-L301 Gene Therapy for Pyruvate Kinase Deficiency. Jul 13, 2020 360
A Combination Therapy of pHRE-Egrl-HSV-TK/Anti-CD133McAb-[sup.131]I/MFH Mediated by FePt Nanoparticles for Liver Cancer Stem Cells. Lin, Mei; Xiao, Yanhong; Jiang, Xingmao; Zhang, Jun; Guo, Ting; Shi, Yujuan Jun 30, 2020 8760
uniQure, CSL Behring enter license agreement for hemophilia B gene therapy. Jun 24, 2020 462
Catalyst Biosciences presents preclinical FIX gene therapy data. Jun 19, 2020 248
Sarepta SRP-9001 results show continued safety, tolerability in four patients. Jun 15, 2020 335
Axovant completes enrollment of low-dose cohort in Phase 1/2 AXO-AAV-GM1 stusy. Jun 8, 2020 278
Sarepta announces expression, functional data from SRP-9003 gene therapy trail. Jun 8, 2020 507
Mobilized Stem Cells Shown Effective In Gene Therapy. Jun 1, 2020 556
The future of Inherited Hemoglobin Disorders-Gene Therapy. Hussain, Abbas Ali; Ullah, Muhammad Anzar; Tahir, Amber Letter to the editor May 29, 2020 922
Pfizer announces updated preliminary data on DMD gene therapy. May 15, 2020 242
Avrobio Reports Updated Clinical Data from Investigational Gene Therapy Programs for Fabry Disease and Cystinosis. May 14, 2020 920
Solid Biosciences presents data from DMD Gene Therapy Program. May 14, 2020 294
Orgenesis leads the charge at an exciting time for cell and gene therapy. May 13, 2020 1233
Homology Medicines announces presentations on in vivo gene therapy, gene editing. May 12, 2020 685
Otonomy, AGTC present preclinical results from gene therapy collaboration. May 12, 2020 205
Orgenesis sees 1Q revenue rocket driven by its Cell and Gene Therapy Biotech platform. Financial report May 12, 2020 803
Sarepta, Dyno Therapeutics to develop gene therapy vectors for muscle diseases. May 11, 2020 179
Cell and Gene Therapies a USD 3.8bn Market Despite COVID-19 Crisis, Report Says. Report May 8, 2020 375
Passage Bio expands gene therapy collaboration with University of Pennsylvania. May 7, 2020 162
Orgenesis leads the charge at an exciting time for cell and gene therapy. May 7, 2020 1201
Mustang Bio receives ATMP classification for MB-107 lentiviral gene therapy. Apr 20, 2020 216
Genprex gene therapy candidate Oncoprex fast-tracking for non-small cell lung cancer treatment. Apr 8, 2020 1507
Daiichi Sankyo, Ultragenyx enter gene therapy manufacturing partnership. Mar 31, 2020 250
Generation Bio and Vir biotechnology Will on Research to Leverage Scalable Non-Viral Gene Therapy Platform for Use Against SARS-CoV-2Coronavirus. Mar 31, 2020 526
RenovaCare says study underway of spray-on gene therapy with SkinGun. Medical condition overview Mar 30, 2020 204
REHABILITATION OR ENHANCEMENT? FDA & THE GENE THERAPIES OF TOMORROW. Harding, Alexander Mar 22, 2020 8670
Next phase of cell and gene therapy manufacture centre to get under way. COREENA FORD Senior Business Reporter coreena.ford@ncjmedia.co.uk Mar 19, 2020 466
French Gene Therapy Specialist Horama Signs Exclusive License Agreement with Leiden University Medical Center. Mar 19, 2020 396
Homology Medicines announces publication of HMI-102 gene therapy data. Mar 16, 2020 213
PsiOxus Therapeutics Starts Clinical Trial with Third Cancer Gene Therapy Treatment. Mar 6, 2020 276
IF DNA IS LIKE SOFTWARE, CAN WE JUST FIX THE CODE? IN A RACE TO CURE HIS DAUGHTER'S ULTRA-RARE DISEASE, A GOOGLE PROGRAMMER ENTERS THE WORLD OF INDIVIDUALIZED DRUGS. Hayden, Erika Check Mar 1, 2020 1886
p19Arf sensitizes B16 melanoma cells to interferon-[beta] delivered via mesenchymal stem cells in vitro. Da-Costa, R.C.; Vieira, I.L.; Hunger, A.; Tamura, R.E.; Strauss, B.E. Mar 1, 2020 4236
Increased Temperature Facilitates Adeno-Associated Virus Vector Transduction of Colorectal Cancer Cell Lines in a Manner Dependent on Heat Shock Protein Signature. Bienkowska, Alicja; Kuzmicka, Weronika; Ciepiela, Olga; Ochocki, Justyn; Malecki, Maciej Mar 1, 2020 7892
Gene therapy saves Emirati siblings from blindness. Ismail Sebugwaawo Feb 25, 2020 607
UAE's first gene therapy improves eyesight of two Emirati sisters. Samihah Zaman, Staff Reporter Feb 25, 2020 302
Orgenesis teams up with Johns Hopkins University to develop gene therapies with its POCare platform. Feb 20, 2020 392
Efficacy of Ultrasound Microbubble-HGF Complex for Treating Hepatic Fibrosis and its Relation with Perfusion Weighted Imaging. Shou-Hong Zhang, Ying Zhang, Kun-Ming Wen, Wei Wu and Wen-Yan Li Feb 14, 2020 3625
Genprex and University of Pittsburgh Sign Exclusive License Agreement for Potentially Curative Gene Therapy Candidate for Diabetes. Feb 13, 2020 589
Genprex inks license agreement with university researchers for potentially curative diabetes gene therapy. Feb 12, 2020 479
Sirion Biotech Licenses Adenovirus Technology to Danish Startup, InProTher for its Novel. Feb 7, 2020 504
Urovant Sciences Publishes Results from Phase 1 Clinical Trials Evaluating URO-902 Gene Therapy in Patients with Overactive Bladder. Feb 7, 2020 482
MaxCyte in 'exceptional position to benefit from explosive growth in gene therapy'. Feb 5, 2020 173
Afghan hero's bid to raise [pounds sterling]2.5m to help treat daughter's rare genetic disorder; EXCLUSIVE: Major Chris Brannigan is on a mission to raise money for new gene therapy for his eight-year-old daughter Hasti which may transform her life. By, Sean Rayment Feb 1, 2020 1009
Seelos Therapeutics to test Parkinson's Disease drug SLS-007 in gene therapy study. Jan 29, 2020 399
Applied Genetic Slumps Despite Encouraging Data For Gene Therapy To Treat Rare Inherited Visual Disorder. Shanthi Rexaline Clinical report Jan 23, 2020 288
Genprex wins FDA FTD for Gene Therapy targeting lung cancer. Jan 22, 2020 211
Genprex wins FDA FTD for Gene Therapy targeting lung cancer. Jan 22, 2020 207
Penny Stock Rips 260% Higher On Fast Track Designation For Experimental Lung Cancer Gene Therapy. Shanthi Rexaline Jan 21, 2020 339
Global Viral Vectors Market Analysis, Drivers & Challenges During the Forecast Period, 2020-2024. Jan 21, 2020 761
ASC Therapeutics partners with Vigene for gene therapy development and manufacturing. Jan 15, 2020 214
ASC Therapeutics partners with Vigene for gene therapy development and manufacturing. Jan 15, 2020 210
PreveCeutical beefs up type 2 diabetes-targeting Dual Gene Therapy program with new siRNA construct. Jan 15, 2020 338
PreveCeutical Announces Further Updates to the Successful Engineering & Cell-Based Efficacy Screening of its Smart-siRNA Constructs for its Dual Gene Therapy Research Program. Jan 14, 2020 1298
Muscle Researchers Discover New Subtype Of Muscle Stem Cells: Findings Could Lead To Development Of Gene Therapies. Jan 13, 2020 815
Orgenesis adds UC Davis to its point-of-care network for developing cell, gene therapy products. Jan 11, 2020 670
Applied Genetic Shares Rip Higher After Eye Disorder Gene Therapy Aces Midstage Trial. Shanthi Rexaline Jan 9, 2020 504
Gene Therapy Breakthrough Could Treat Kidney Diseases. Johnny Vatican Jan 7, 2020 402
Global Gene Therapy Market Outlook and Projections, 2019-2027, Featuring Profiles of the Top 5 Players: Novartis, Amgen, Orchard Therapeutics, Kite Pharma, and uniQure. Jan 7, 2020 659
Researchers test novel approach for injecting gene therapy vectors into kidney. ANI Jan 5, 2020 386
Study suggests feasibility of treating encephalopathy with gene therapy. ANI Jan 5, 2020 278
Gene Therapy May Be Long-Term Cure for Type of Hemophilia. Dennis Thompson, HealthDay Reporter Jan 2, 2020 649
Researchers experiment with gene therapy vector injections to cure renal disease. ANI Jan 1, 2020 400
Biological Characteristics and Carrier Functions of Pegylated Manganese Zinc Ferrite Nanoparticles. Guo, Ting; Dou, Fengxiao; Lin, Mei; Huang, Junxing; Zhou, Chenglin; Zhang, Jun; Yu, Hong; Jiang, Xin Dec 31, 2019 5934
New technology allows gene therapy dose regulation. ANI Dec 26, 2019 788
Sangamo reports transfer of SB-525 Hemophilia A Gene Therapy IND. Dec 24, 2019 187
Sangamo Completes Early Transfer to Pfizer of SB-525 Hemophilia A Gene Therapy IND and an Earned USD 25m Milestone Payment. Dec 24, 2019 268
A New Gene Therapy Strategy. Dec 24, 2019 927
Sangamo reports transfer of SB-525 Hemophilia A Gene Therapy IND. Dec 24, 2019 191
Sarepta, Roche Strike Gene Therapy Licensing Agreement Worth Up To $2.85B. Shanthi Rexaline Dec 23, 2019 526
The Daily Biotech Pulse: Axovant Surges On Gene Therapy Study Results, FDA Approves Merck's Ebola Vaccine, Abeona Announces Offering. Shanthi Rexaline Dec 20, 2019 1027
The Daily Biotech Pulse: Positive Adcom Verdict For Merck, Homology Medicine Slips On Mixed Gene Therapy Efficacy Data. Shanthi Rexaline Dec 18, 2019 1056
Homology Medicines' Gene Therapy For Phenylketonuria Found Safe, Efficacy Data Mixed. Shanthi Rexaline Dec 18, 2019 405
Rocket Pharmaceuticals Receives the European Medicines Agency PRIME Eligibility for RP-L102 Gene Therapy for Fanconi Anemia. Dec 17, 2019 771
Ocugen looking to lead the way with their new gene therapy platform. Dec 12, 2019 110
Global Gene Therapy Market Report, 2019-2024: Analysis on Cancer, Metabolic Disorders, Eye Disorders, Spinal Muscular Atrophy, and Other Indications. Report Dec 9, 2019 867
Orgenesis and Theracell to launch point-of-care cell and gene therapy centers in HYGEIA Group's hospitals. Dec 7, 2019 607
Gene Therapy Market 2019-2025 / Size, Share, Trends, Growth Opportunities, Segmentation, Competitive Landscape and Regional Analysis. Dec 6, 2019 873
Global Type 1 Diabetes Market Report 2019: T1D Insulin Gene Therapy and Immuno-modulators Dominate First-in-Class Pipeline with Novel Target Classes Demonstrating Potential Beta-Cell Regeneration. Report Dec 3, 2019 817
Japan's Astellas To Buy Gene Therapy Company Audentes For $3B Cash. Shanthi Rexaline Dec 3, 2019 580
The Gene Therapy Names Moving On The Audentes Buyout Deal. Shanthi Rexaline Dec 3, 2019 559
Dyno Therapeutics Highlights Research Published in Science Enabling Artificial Intelligence Approach to Create New AAV Capsids for Gene Therapies. Dec 3, 2019 567
VLPs Derived from the CCMV Plant Virus Can Directly Transfect and Deliver Heterologous Genes for Translation into Mammalian Cells. Villagrana-Escareno, Maria V.; Reynaga-Hernandez, Elizabeth; Galicia-Cruz, Othir G.; Duran-Meza, Ana Nov 30, 2019 7488
Therapeutic Strategies for Attenuation of Retinal Ganglion Cell Injury in Optic Neuropathies: Concepts in Translational Research and Therapeutic Implications. Fu, Lin; Kwok, Sum Sum; Chan, Yau Kei; Lai, Jimmy Shiu Ming; Pan, Weihua; Nie, Li; Shih, Kendrick Co Nov 30, 2019 8373
Lonza signs strategic collaboration with DiNAQOR. Nov 28, 2019 151
Lonza signs strategic collaboration with DiNAQOR. Nov 28, 2019 147
Global Viral Vectors, Non-Viral Vectors & Gene Therapy Manufacturing Industry Outlook (2019-2030): Focus on Contract Manufacturers & Companies with In-house Manufacturing Facilities. Industry overview Nov 27, 2019 1089
Ferring and Blackstone Life Sciences Invest Over $570 Million USD in Novel Gene Therapy for Bladder Cancer Patients. Nov 26, 2019 1551
Gene Therapy Market Expected to Grow with a CAGR of 16.92% During the Forecast Period, 2019-2024. Nov 26, 2019 793
Global Gene Therapy Market to reach at CAGR of 40.7% during the forecast period of 2019 to 2025 / Size, Share, Trends, Growth Opportunities, Segmentation, Competitive Landscape and Regional Analysis. Nov 22, 2019 823
Biogen Announces Enrollment Completion of Global Phase 3 Gene Therapy Study for an Inherited Retinal Disorder. Clinical report Nov 21, 2019 1368
HMC team uses gene therapy to treat congenital spinal muscular atrophy. Nov 20, 2019 640
Global Cell & Gene Therapy Market Outlook and Forecast 2019-2024 - Robust Pipeline Products & Increasing Funding for R&D Activities Trigger Massive Growth. Nov 20, 2019 983
HMC achieves rare distinction with gene therapy breakthrough. Nov 19, 2019 1034
Gene Therapy in Neurology, 2019: Market Outlook, Pipeline Assessment, Unmet Needs, Barriers, Key Company Strategies & Payer Perspective. Nov 12, 2019 1305
Solid Biosciences Shares Crash To Record Low After FDA Places Gene Therapy Program On Hold. Shanthi Rexaline Nov 12, 2019 449
Gene therapy may help reverse blindness. Nov 8, 2019 277
Orchard Therapeutics to present registrational data on gene therapies. Nov 6, 2019 662
Cryoport and Lonza announce partnership in cell and gene therapy field. Nov 5, 2019 135
Advanced Textbook on Gene Transfer, Gene Therapy and Genetic Pharmacology: Principles, Delivery and Pharmacological and Biomedical Applications of Nucleotide-Based Therapies, 2nd Edition. Brief article Nov 1, 2019 143
Lentiviral Gene Therapy Appears Effective in X-CGD. Bowser, Andrew D. Nov 1, 2019 460
Transitioning from Clinical Production to Commercial Manufacturing: Cell and gene therapy facilities face a unique set of challenges as they scale towards commercial production and require equally unique solutions. Walters, Peter Nov 1, 2019 2069
Aldevron, NTC Team Up for Gene Therapy Manufacturing. Nov 1, 2019 331
Recombinant deoxyribonucleoside kinase from Drosophila melanogaster can improve gemcitabine based combined gene/chemotherapy for targeting cancer cells. Fatima, Mahak; Ahmed, Muhammad Mubashar Iqbal; Batool, Faiza; Riaz, Anjum; Ali, Moazzam; Munch-Peter Report Nov 1, 2019 5371
The Global Viral Vector Vaccines Manufacturing Market is Expected to Grow at a CAGR of 18.19% by 2027. Oct 31, 2019 673
Catalent to Discuss Accelerating Development in Biologics and Gene Therapies. Oct 30, 2019 727
New KUBio box for viral vectors boosts gene therapy manufacturing. Oct 28, 2019 786
Amicus announces additional interim clinical data for CLN6 gene therapy. Oct 24, 2019 377
Catalent to Debate Delivery & Transportation Logistics of Cell & Gene Therapies. Oct 23, 2019 401
Homology Medicines presents data from investigational gene therapy programs. Oct 21, 2019 331
Plant Compound Added To Gene Therapy May Speed Up Treatments. Oct 21, 2019 670
Eyevensys Presents Initial Data from Phase I/II Trial of Innovative, Non-Viral Gene Therapy for Ocular Diseases at 11th Annual Ophthalmology Innovation Summit. Oct 18, 2019 637
Creative Biolabs Announces One-stop Services about Adenovirus Vector. Oct 17, 2019 610
Astellas Pharma Inc. - Astellas Commits Nearly $13 Million to Fund Boston-area Start-Up Innovation in Cell and Gene Therapy - Financial support for LabCentral Incubators builds on Astellas' $1 Billion+ investment in Boston's Life Science Community -- 1/10/2019. Oct 16, 2019 426
Gene Therapy Market Analysis, Trends, and Forecasts, 2025. Oct 15, 2019 492
Gene therapy effective for treating wet age-related macular degeneration: Study. ANI Oct 14, 2019 522
Global Neurodegenerative Disorder Therapeutics Market 2019-2024: Opportunities in Digital Biomarkers, Microbiome Therapeutics, Cell and Gene Therapy, Drug Delivery, Drug Repurposing. Oct 14, 2019 958
Viral Vector & Plasmid DNA Report 2019: Technologies and Global Markets, 2018-2024. Report Oct 10, 2019 1221
Global Gene Therapy Technologies, Companies & Markets During the Forecast Period, 2018-2028. Oct 9, 2019 768
The Daily Biotech Pulse: D-Day For Clinuvel, Qiagen Warns Of Q3 Shortfall, Prevail Announces Gene Therapy Collaboration. Shanthi Rexaline Oct 8, 2019 950
Avrobio doses first patient in Phase 1/2 trial of gene therapy for cystinosis. Oct 8, 2019 155
Genprex believes in non-viral delivery as the next evolution in gene therapy, and scientific paper agrees. Oct 8, 2019 468
Astellas Pharma Inc. - Astellas Commits Nearly $13 Million to Fund Boston-area Start-Up Innovation in Cell and Gene Therapy - Financial support for LabCentral Incubators builds on Astellas' $1 Billion+ investment in Boston's Life Science Community - 1/10/2019. Oct 8, 2019 426
Sarepta announces results from gene therapy trial for beta-sarcoglycanopathy. Oct 4, 2019 216
Sarepta data 'de-risk' entire LGMD gene therapy platform, says Piper Jaffray. Oct 4, 2019 135
William Blair says new data shows Sarepta's gene therapy pipeline breadth. Oct 4, 2019 101
BioMarin Pharmaceutical Inc. (NASDAQ: BMRN) - BioMarin, Pioneer in Phenylketonuria (PKU) Therapies, Submits Clinical Trial Application (CTA) in U.K. for Investigational Gene Therapy for PKU -- 26/9/2019. Oct 2, 2019 531

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