Regulus Therapeutics receives orphan drug designation for RG-012.
M2 EQUITYBITES-July 23, 2014-Regulus Therapeutics receives orphan drug designation for RG-012
(C)2014 M2 COMMUNICATIONS http://www.m2.com
Regulus Therapeutics, a United States-based biopharmaceutical company, has received orphan drug designation for its RG-012, a single stranded, chemically modified oligonucleotide from the US Food and Drug Administration, it was reported yesterday.
The product binds to and inhibits the function of microRNA-21 (miR-21), as a therapeutic to treat Alport syndrome, a genetic kidney disease.
The firm is planning to start a natural history of disease trial to gather further information about the progression of Alport syndrome and to inform future clinical development plans of RG-012, a key programme under its 'Clinical Map Initiative'. Regulus chief medical officer, Paul Grint, stated that the company is happy to secure orphan drug designation for RG-012 and are encouraged by the FDA's recognition for the need of new treatments like microRNA therapeutics for rare and orphan diseases, such as Alport syndrome.
((Comments on this story may be sent to email@example.com))
|Printer friendly Cite/link Email Feedback|
|Publication:||M2 EquityBites (EQB)|
|Date:||Jul 23, 2014|
|Previous Article:||Russia's Hals-Development buys minority stake in CLG.|
|Next Article:||Arena Pharmaceuticals' subsidiary signs marketing and supply contract with Abic Marketing.|